"Scientists have used gene therapy to halt the progression of adrenoleukodystrophy, a fatal neurodegenerative disease caused by a single defective gene, in two seven-year-old boys.""It took more than a decade to refine the therapy, in which stem cells taken from the boys’ bone marrow were hacked with healthy copies of the gene, then returned to their bodies. Without them, the boys would soon be dead."
[image and text from http://www.wired.com/wiredscience/2009/11/ald-gene-therapy/]
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